The new gene therapy directly targets hematopoietic stem cells and no longer requires transplantation.

New Gene Therapy Directly Targets Hematopoietic Stem Cells, No Longer Requiring Transplantation

via cnBeta.COM Chinese Industry Information Station - Telegram Channel

Telegraph
New Gene Therapy Directly Targets Hematopoietic Stem Cells, No Longer Requiring Transplantation

The new gene therapy directly targets hematopoietic stem cells and no longer requires transplantation. The illustration shows how the efficient transport of blood stem cells in the early postnatal blood circulation contributes to lentiviral vector-mediated in vivo gene transfer. Credit: Ella Maru Studio. This study, published in the journal Nature, opens up new possibilities for treating certain inherited blood diseases without the need for stem cell transplantation or chemotherapy. SR-Tiget is internationally renowned for its leading position in the field of lentiviral vector gene therapy and has an outstanding track record in translating advanced research into clinical treatments. The study was led by Dr. Michela Milani and co-authored by Professor Luigi Naldini, Director of SR-Tiget, and Alessio…